Correction of β-thalassemia major by gene transfer in haematopoietic progenitors of pediatric patientsEMBO Molecular Medicine
Volume 2, Issue 8, August 2010, Pages: 315–328, Emanuela Anna Roselli, Riccardo Mezzadra, Marta Claudia Frittoli, Giulietta Maruggi, Erika Biral, Fulvio Mavilio, Fabrizio Mastropietro, Antonio Amato, Giovanni Tonon, Chiara Refaldi, Maria Domenica Cappellini, Marco Andreani, Guido Lucarelli, Maria Grazia Roncarolo, Sarah Marktel and Giuliana Ferrari
Article first published online : 21 JUL 2010, DOI: 10.1002/emmm.201000083