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There are 7932320 results for: content related to: Hepatic gene therapy using lentiviral vectors: Has safety been established?

  1. Gene therapy strategies for hemophilia: benefits versus risks

    The Journal of Gene Medicine

    Volume 12, Issue 10, October 2010, Pages: 797–809, Inge Petrus, Marinee Chuah and Thierry VandenDriessche

    Version of Record online : 16 SEP 2010, DOI: 10.1002/jgm.1500

  2. You have free access to this content
    Gene therapy for hemophilia

    Journal of Thrombosis and Haemostasis

    Volume 11, Issue s1, June 2013, Pages: 99–110, M. K. Chuah, H. Evens and T. VandenDriessche

    Version of Record online : 30 JUN 2013, DOI: 10.1111/jth.12215

  3. You have free access to this content
    Hepatic lentiviral gene transfer is associated with clonal selection, but not with tumor formation in serially transplanted rodents

    Hepatology

    Volume 58, Issue 1, July 2013, Pages: 397–408, Ina Rittelmeyer, Michael Rothe, Martijn H. Brugman, Marcus Iken, Axel Schambach, Michael P. Manns, Christopher Baum, Ute Modlich and Michael Ott

    Version of Record online : 27 MAY 2013, DOI: 10.1002/hep.26204

  4. Gene therapy for monogenic disorders of the bone marrow

    British Journal of Haematology

    Volume 171, Issue 2, October 2015, Pages: 155–170, Sujal Ghosh, Adrian J. Thrasher and H. Bobby Gaspar

    Version of Record online : 5 JUN 2015, DOI: 10.1111/bjh.13520

  5. Gene therapy approaches for lysosomal storage disorders, a good model for the treatment of mendelian diseases

    Acta Paediatrica

    Volume 101, Issue 7, July 2012, Pages: 692–701, Rosella Tomanin, Alessandra Zanetti, Eva Zaccariotto, Francesca D’Avanzo, Cinzia M Bellettato and Maurizio Scarpa

    Version of Record online : 11 APR 2012, DOI: 10.1111/j.1651-2227.2012.02674.x

  6. The Australasian Gene Therapy Society

    The Journal of Gene Medicine

    Volume 7, Issue 8, August 2005, Pages: 1113–1143,

    Version of Record online : 2 AUG 2005, DOI: 10.1002/jgm.808

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    Gene therapy for hemophilia: an imperative to succeed

    Journal of Thrombosis and Haemostasis

    Volume 3, Issue 6, June 2005, Pages: 1195–1205, C. HOUGH and D. LILLICRAP

    Version of Record online : 9 JUN 2005, DOI: 10.1111/j.1538-7836.2005.01401.x

  8. Organ targeted prenatal gene therapy—how far are we?

    Prenatal Diagnosis

    Volume 31, Issue 7, July 2011, Pages: 720–734, Vedanta Mehta, Khalil Abi Nader, Simon Waddington and Anna L David

    Version of Record online : 25 MAY 2011, DOI: 10.1002/pd.2787

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    Liver-targeted gene therapy: Approaches and challenges

    Liver Transplantation

    Volume 21, Issue 6, June 2015, Pages: 718–737, Rajagopal N. Aravalli, John D. Belcher and Clifford J. Steer

    Version of Record online : 26 MAY 2015, DOI: 10.1002/lt.24122

  10. You have full text access to this OnlineOpen article
    Hepatocyte-targeted expression by integrase-defective lentiviral vectors induces antigen-specific tolerance in mice with low genotoxic risk

    Hepatology

    Volume 53, Issue 5, May 2011, Pages: 1696–1707, Janka Mátrai, Alessio Cantore, Cynthia C. Bartholomae, Andrea Annoni, Wei Wang, Abel Acosta-Sanchez, Ermira Samara-Kuko, Liesbeth De Waele, Ling Ma, Pietro Genovese, Martina Damo, Anne Arens, Kevin Goudy, Timothy C. Nichols, Christof von Kalle, Marinee K. L. Chuah, Maria Grazia Roncarolo, Manfred Schmidt, Thierry VandenDriessche and Luigi Naldini

    Version of Record online : 22 APR 2011, DOI: 10.1002/hep.24230

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    A review of gene therapy for haematological disorders

    British Journal of Haematology

    Volume 128, Issue 1, January 2005, Pages: 3–17, Amit C. Nathwani, Andrew M. Davidoff and David C. Linch

    Version of Record online : 5 NOV 2004, DOI: 10.1111/j.1365-2141.2004.05231.x

  12. The 12th Annual Meeting 2006 Japan Society of Gene Therapy

    The Journal of Gene Medicine

    Volume 8, Issue 12, December 2006, Pages: 1436–1475,

    Version of Record online : 27 NOV 2006, DOI: 10.1002/jgm.988

  13. Preclinical Safety Evaluation of Biopharmaceuticals

    Preclinical Safety Evaluation of Biopharmaceuticals: A Science-Based Approach to Facilitating Clinical Trials

    Mercedes A. Serabian, Ying Huang, Pages: 713–747, 2007

    Published Online : 14 NOV 2007, DOI: 10.1002/9780470292549.ch32

  14. The 11th Annual Meeting of the Japan Society of Gene Therapy 2005

    The Journal of Gene Medicine

    Volume 8, Issue 3, March 2006, Pages: 370–408,

    Version of Record online : 28 FEB 2006, DOI: 10.1002/jgm.873

  15. RH10 provides superior transgene expression in mice when compared with natural AAV serotypes for neonatal gene therapy

    The Journal of Gene Medicine

    Volume 12, Issue 9, September 2010, Pages: 766–778, Chuhong Hu, Ronald W. Busuttil and Gerald S. Lipshutz

    Version of Record online : 1 SEP 2010, DOI: 10.1002/jgm.1496

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    6th Australasian Gene Therapy Society Meeting

    The Journal of Gene Medicine

    Volume 11, Issue 9, September 2009, Pages: 834–856,

    Version of Record online : 21 AUG 2009, DOI: 10.1002/jgm.1375

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    Hepatocyte-based gene therapy

    Journal of Hepato-Biliary-Pancreatic Surgery

    Volume 8, Issue 1, February 2001, Pages: 51–57, Chandan Guha, Namita Roy-Chowdhury, Hugo Jauregui and Jayanta Roy-Chowdhury

    Version of Record online : 1 FEB 2001, DOI: 10.1007/s005340170050

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    Changing channels in pain and epilepsy: Exploiting ion channel gene therapy for disorders of neuronal hyperexcitability

    FEBS Letters

    Volume 589, Issue 14, June 22, 2015, Pages: 1620–1634, Albert Snowball and Stephanie Schorge

    Version of Record online : 12 MAY 2015, DOI: 10.1016/j.febslet.2015.05.004

  19. Gene therapy for immune tolerance induction in hemophilia with inhibitors

    Journal of Thrombosis and Haemostasis

    Volume 14, Issue 6, June 2016, Pages: 1121–1134, V. R. Arruda and B. J. Samelson-Jones

    Version of Record online : 14 MAY 2016, DOI: 10.1111/jth.13331

  20. Liver-Directed Gene Therapy

    The Liver: Biology and Pathobiology, Fifth Edition

    Betsy T. Kren, Clifford J. Steer, Namita Roy Chowdhury, Jayanta Roy Chowdhury, Pages: 965–990, 2009

    Published Online : 6 OCT 2009, DOI: 10.1002/9780470747919.ch59