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There are 10619 results for: content related to: In vitro evaluation of novel antisense oligonucleotides is predictive of in vivo exon skipping activity for Duchenne muscular dystrophy

  1. An octaguanidine–morpholino oligo conjugate improves muscle function of mdx mice

    Muscle & Nerve

    Volume 44, Issue 4, October 2011, Pages: 563–570, Jeffrey J. Widrick, Shan Jiang, Seung Jun Choi, Shannon T. Knuth and Paul A. Morcos

    Version of Record online : 15 SEP 2011, DOI: 10.1002/mus.22126

  2. You have free access to this content
    Progress in therapy for Duchenne muscular dystrophy

    Experimental Physiology

    Volume 96, Issue 11, November 2011, Pages: 1101–1113, Rebecca J. Fairclough, Akshay Bareja and Kay E. Davies

    Version of Record online : 20 SEP 2011, DOI: 10.1113/expphysiol.2010.053025

  3. Development of Antisense-Mediated Exon Skipping as a Treatment for Duchenne Muscular Dystrophy

    Annals of the New York Academy of Sciences

    Volume 1175, Issue 1, September 2009, Pages: 71–79, Hans Heemskerk, Christa L. de Winter, Gert-Jan B. van Ommen, Judith C.T. van Deutekom and Annemieke Aartsma-Rus

    Version of Record online : 24 SEP 2009, DOI: 10.1111/j.1749-6632.2009.04973.x

  4. Dystrophin expression in the mdx mouse after localised and systemic administration of a morpholino antisense oligonucleotide

    The Journal of Gene Medicine

    Volume 8, Issue 2, February 2006, Pages: 207–216, Susan Fletcher, Kaite Honeyman, Abbie M. Fall, Penny L. Harding, Russell D. Johnsen and Steve D. Wilton

    Version of Record online : 14 NOV 2005, DOI: 10.1002/jgm.838

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    In vivo comparison of 2′-O-methyl phosphorothioate and morpholino antisense oligonucleotides for Duchenne muscular dystrophy exon skipping

    The Journal of Gene Medicine

    Volume 11, Issue 3, March 2009, Pages: 257–266, Hans A. Heemskerk, Christa L. de Winter, Sjef J. de Kimpe, Petra van Kuik-Romeijn, Niki Heuvelmans, Gerard J. Platenburg, Gert-Jan B. van Ommen, Judith C. T. van Deutekom and Annemieke Aartsma-Rus

    Version of Record online : 12 JAN 2009, DOI: 10.1002/jgm.1288

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    Ex Vivo Gene Editing of the Dystrophin Gene in Muscle Stem Cells Mediated by Peptide Nucleic Acid Single Stranded Oligodeoxynucleotides Induces Stable Expression of Dystrophin in a Mouse Model for Duchenne Muscular Dystrophy

    STEM CELLS

    Volume 32, Issue 7, July 2014, Pages: 1817–1830, Farnoosh Nik-Ahd and Carmen Bertoni

    Version of Record online : 17 JUN 2014, DOI: 10.1002/stem.1668

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    By-passing the nonsense mutation in the 4CV mouse model of muscular dystrophy by induced exon skipping

    The Journal of Gene Medicine

    Volume 11, Issue 1, January 2009, Pages: 46–56, Chalermchai Mitrpant, Sue Fletcher, Patrick L. Iversen and Steve D. Wilton

    Version of Record online : 12 NOV 2008, DOI: 10.1002/jgm.1265

  8. Exon-skipping therapy for Duchenne muscular dystrophy

    Neuropathology

    Volume 29, Issue 4, August 2009, Pages: 494–501, Akinori Nakamura and Shin'ichi Takeda

    Version of Record online : 22 MAY 2009, DOI: 10.1111/j.1440-1789.2009.01028.x

  9. Cardiac and Respiratory Dysfunction in Duchenne Muscular Dystrophy and the Role of Second Messengers

    Medicinal Research Reviews

    Volume 33, Issue 5, September 2013, Pages: 1174–1213, Matias Mosqueira, Ulrike Zeiger, Moritz Förderer, Heinrich Brinkmeier and Rainer HA Fink

    Version of Record online : 30 APR 2013, DOI: 10.1002/med.21279

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    Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment

    EMBO reports

    Volume 5, Issue 9, September 2004, Pages: 872–876, Kristen J Nowak and Kay E Davies

    Version of Record online : 1 SEP 2004, DOI: 10.1038/sj.embor.7400221

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    Effects of stretch-activated channel blockers on [Ca2+]i and muscle damage in the mdx mouse

    The Journal of Physiology

    Volume 562, Issue 2, January 2005, Pages: 367–380, Ella W. Yeung, Nicholas P. Whitehead, Thomas M. Suchyna, Philip A. Gottlieb, Frederick Sachs and David G. Allen

    Version of Record online : 7 JAN 2005, DOI: 10.1113/jphysiol.2004.075275

  12. Gene and cell-mediated therapies for muscular dystrophy

    Muscle & Nerve

    Volume 47, Issue 5, May 2013, Pages: 649–663, Patryk Konieczny, Kristy Swiderski and Jeffrey S. Chamberlain

    Version of Record online : 28 MAR 2013, DOI: 10.1002/mus.23738

  13. Peptide-Morpholino Conjugate: A Promising Therapeutic for Duchenne Muscular Dystrophy

    Annals of the New York Academy of Sciences

    Volume 1175, Issue 1, September 2009, Pages: 55–60, Hong M. Moulton, Bo Wu, Natee Jearawiriyapaisarn, Peter Sazani, Qi Long Lu and Ryszard Kole

    Version of Record online : 24 SEP 2009, DOI: 10.1111/j.1749-6632.2009.04976.x

  14. Adaptive and nonadaptive responses to voluntary wheel running by mdx mice

    Muscle & Nerve

    Volume 38, Issue 4, October 2008, Pages: 1290–1293, Rachel M. Landisch, Allison M. Kosir, Steven A. Nelson, Kristen A. Baltgalvis and Dawn A. Lowe

    Version of Record online : 24 SEP 2008, DOI: 10.1002/mus.21141

  15. Altered mitogen-activated protein kinase signaling in dystrophic (mdx) muscle

    Muscle & Nerve

    Volume 46, Issue 3, September 2012, Pages: 374–383, Gayle M. Smythe and Jade K. Forwood

    Version of Record online : 20 AUG 2012, DOI: 10.1002/mus.23312

  16. ROLE OF CONTRACTION-INDUCED INJURY IN THE MECHANISMS OF MUSCLE DAMAGE IN MUSCULAR DYSTROPHY

    Clinical and Experimental Pharmacology and Physiology

    Volume 31, Issue 8, August 2004, Pages: 557–561, Gordon S Lynch

    Version of Record online : 3 AUG 2004, DOI: 10.1111/j.1440-1681.2004.04026.x

  17. An Amphipathic trans-Acting Phosphorothioate DNA Element Delivers Uncharged PNA and PMO Nucleic Acid Sequences in Mammalian Cells

    Unit

    Current Protocols in Nucleic Acid Chemistry

    4:4.69.1–4.69.22

    Harsh V. Jain and Serge L. Beaucage

    Published Online : 1 MAR 2016, DOI: 10.1002/0471142700.nc0469s64

  18. Protective effect of female gender–related factors on muscle force-generating capacity and fragility in the dystrophic mdx mouse

    Muscle & Nerve

    Volume 48, Issue 1, July 2013, Pages: 68–75, Christophe Hourdé, Pierre Joanne, Phillippe Noirez, Onnik Agbulut, Gillian Butler-Browne and Arnaud Ferry

    Version of Record online : 28 APR 2013, DOI: 10.1002/mus.23700

  19. Suramin attenuates dystrophin-deficient cardiomyopathy in the mdx mouse model of duchenne muscular dystrophy

    Muscle & Nerve

    Volume 48, Issue 6, December 2013, Pages: 911–919, Drielen De Oliveira Moreira, Juliano Alves Pereira, Ana Paula Tiemi Taniguti, Cíntia Yuri Matsumura, Luis Alberto Ferreira Ramos, Miguel Arcanjo Areas, Humberto Santo Neto and Maria Julia Marques

    Version of Record online : 11 SEP 2013, DOI: 10.1002/mus.23858

  20. Effective repetitive dystrophin gene transfer into skeletal muscle of adult mdx mice using a helper-dependent adenovirus vector expressing the coxsackievirus and adenovirus receptor (CAR) and dystrophin

    The Journal of Gene Medicine

    Volume 7, Issue 8, August 2005, Pages: 1010–1022, Yuji Uchida, Yasushi Maeda, En Kimura, Satoshi Yamashita, Yasuto Nishida, Toshiyuki Arima, Teruyuki Hirano, Eiichiro Uyama, Shuji Mita and Makoto Uchino

    Version of Record online : 8 MAR 2005, DOI: 10.1002/jgm.745