the AJMG SEQUENCE
Gene therapy shows potential as Usher syndrome treatment
Translational read-through inducing drugs get past stop codons in type 1c
Article first published online: 24 JUL 2013
Copyright © 2013 Wiley Periodicals, Inc.
American Journal of Medical Genetics Part A
Volume 161, Issue 8, page xi, August 2013
How to Cite
(2013), Gene therapy shows potential as Usher syndrome treatment. Am. J. Med. Genet., 161: xi. doi: 10.1002/ajmg.a.36175
- Issue published online: 24 JUL 2013
- Article first published online: 24 JUL 2013
- 2012. A comparative evaluation of NB30, NB54 and PTC 124 in translational read-through efficacy for treatment of an USH1C nonsense mutation. EMBO Mol Med Nov; 4(11):1186–1199. , , , , , , , .