Original Article

Efficacy of systemic morpholino exon-skipping in duchenne dystrophy dogs†

  1. Toshifumi Yokota PhD1,
  2. Qi-long Lu MD, PhD2,
  3. Terence Partridge PhD1,
  4. Masanori Kobayashi DVM3,
  5. Akinori Nakamura MD, PhD3,
  6. Shińichi Takeda MD, PhD3,*,
  7. Eric Hoffman PhD1,*

Article first published online: 13 MAR 2009

DOI: 10.1002/ana.21627

Issue

Annals of Neurology

Annals of Neurology

Volume 65, Issue 6, pages 667–676, June 2009

Additional Information

How to Cite

Yokota, T., Lu, Q.-l., Partridge, T., Kobayashi, M., Nakamura, A., Takeda, S. and Hoffman, E. (2009), Efficacy of systemic morpholino exon-skipping in duchenne dystrophy dogs. Ann Neurol., 65: 667–676. doi: 10.1002/ana.21627

Author Information

  1. 1

    Research Center for Genetic Medicine, Children's National Medical Center, Washington, DC

  2. 2

    McColl-Lockwood Laboratory for Muscular Dystrophy Research, Neuromuscular/Amyotrophic Lateral Sclerosis Center, Carolinas Medical Center, Charlotte, NC

  3. 3

    Department of Molecular Therapy, National Institute of Neuroscience, National Center of Neurology and Psychiatry, Kodaira, Tokyo, Japan

*Department of Molecular Therapy National Institute of Neuroscience, National Center of Neurology and Psychiatry 4-1-1 Ogawa-higashi, Kodaiva, Tokyo, Japan

  1. †

    Potential conflict of interest: Nothing to report.

Publication History

  1. Issue published online: 25 JUN 2009
  2. Article first published online: 13 MAR 2009
  3. Manuscript Accepted: 5 DEC 2008
  4. Manuscript Revised: 29 NOV 2008
  5. Manuscript Received: 1 JUL 2008

Funded by

  • Foundation to Eradicate Duchenne
  • Department of Defense CDMRP program. Grant Number: W81XWH-05-1-0616
  • Jain Foundation
  • Crystal Ball of Virginia Beach (Muscular Dystrophy Association USA)
  • National Center for Medical Rehabilitation Research. Grant Number: 5R24HD050846-02
  • NIH Wellstone Muscular Dystrophy Research Centers. Grant Number: IU54HD053177-01A1
  • Ministry of Health, Labor, and Welfare of Japan (Research on Nervous and Mental Disorders). Grant Numbers: 16B-2, 19A-7
  • Ministry of Health, Labor, and Welfare of Japan (Health and Labor Sciences, Research Grants for Translation Research; Health Sciences Research Grants for Research on Psychiatry and Neurological Disease and Mental Health). Grant Numbers: H19-translational research-003, H18-kokoro-019

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