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By-passing the nonsense mutation in the 4CV mouse model of muscular dystrophy by induced exon skipping

  1. Chalermchai Mitrpant1,2,
  2. Sue Fletcher1,
  3. Patrick L. Iversen3,
  4. Steve D. Wilton1,*

Article first published online: 12 NOV 2008

DOI: 10.1002/jgm.1265

Issue

The Journal of Gene Medicine

The Journal of Gene Medicine

Volume 11, Issue 1, pages 46–56, January 2009

Additional Information

How to Cite

Mitrpant, C., Fletcher, S., Iversen, P. L. and Wilton, S. D. (2009), By-passing the nonsense mutation in the 4CV mouse model of muscular dystrophy by induced exon skipping. J. Gene Med., 11: 46–56. doi: 10.1002/jgm.1265

Author Information

  1. 1

    Centre for Neuromuscular and Neurological Disorders, University of Western Australia, QE II Medical Centre, Nedlands, Australia

  2. 2

    Department of Biochemistry, Faculty of Medicine, Siriraj Hospital, Mahidol University, Bangkok, Thailand

  3. 3

    AVI Biopharma, Corvallis, OR, USA

*Centre for Neuromuscular and Neurological Disorders, University of Western Australia, QE II Medical Centre, Nedlands, Western Australia, 6009, Australia.

Publication History

  1. Issue published online: 29 DEC 2008
  2. Article first published online: 12 NOV 2008
  3. Manuscript Accepted: 25 SEP 2008
  4. Manuscript Revised: 2 AUG 2008
  5. Manuscript Received: 29 MAY 2008

Funded by

  • National Institutes of Health. Grant Number: RO1 NS044146
  • Muscular Dystrophy Association USA. Grant Number: MDA3718
  • National Health and Medical Research Council of Australia. Grant Number: 303216

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    Carl F. Adkin, Penelope L. Meloni, Susan Fletcher, Abbie M. Adams, Francesco Muntoni, Brenda Wong, Steve D. Wilton, Multiple exon skipping strategies to by-pass dystrophin mutations, Neuromuscular Disorders, 2012, 22, 4, 297

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